R&D Pipeline · RECORNA

Accelerating Novel Therapies
For Unmet Needs

Development Progress

CNS-Targeted Therapies
Population
Indication
Mechanism
DiscoveryPreclinicalIITClinical
Dravet Syndrome / SCN1A
mRNA upregulation
Neurodegenerative Diseases
Introduce a protective mutation
Liver-Targeted Therapies
Population
Indication
Mechanism
DiscoveryPreclinicalIITClinical
Rare Metabolic Diseases
repair a pathogenic vatiant
Metabolic Disorders
mRNA upregulation
Cardiovascular Diseases
mRNA Upregulation
Anti-Aging Research
Introduce a beneficial mutation